Explore the latest insights, breakthroughs, and stories shaping our journey towards innovative research and advancements in STXBP1 and Single Gene disorders on Rafa’s Moonshot Blog.

Did you know? The tiny C. elegans worm shares 60-80% of its genes with humans, making it an invaluable tool in genetic research. At Rafa’s Moonshot, we’re using these remarkable creatures, among other models, to pave the way for breakthrough treatments for STXBP1 disorders. When it comes to finding a…
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